Biomarin’s hemophilia gene therapy nears European market after US setback
A single dose of the US-based biotech firm’s drug could be enough for a lifelong treatment of the rare bleeding disorder – but Roctavian’s price tag is making governments around the world think twice.
By James Paton, bloomberg
Biomarin Pharmaceutical Inc. expects European patients to begin receiving its gene therapy for a life-threatening blood-clotting disorder before the end of the year, raising the drugmaker’s hopes it can succeed where rival Bluebird Bio Inc. faltered.
Already a subscriber?Log in here
Read the whole article
Get access for 14 days for free. No credit card is needed, and you will not be automatically signed up for a paid subscription after the free trial.
