MedWatch

Voxzogo demonstrates positive results for infants with dwarfism

Biomarin’s achondroplasia treatment has been approved for children as young as five in the US, and the firm is now hoping to address patients who have yet to turn one.

Photo: LUKAS BARTH/REUTERS / X03379

In November 2021, the US Food and Drug Administration (FDA) market approved Biomarin’s drug, Voxzogo (vosoritide), for five-year-old children and up who have achondroplasia, also known as dwarfism.

The company has now publicized results from a phase II study that included patients with the disease younger than one year of age, according to a press release.

Already a subscriber? Log in.

Read the whole article

Get access for 14 days for free.
No credit card is needed, and you will not be automatically signed up for a paid subscription after the free trial.

  • Access all locked articles
  • Receive our daily newsletters
  • Access our app
An error has occured. Please try again later.

Get full access for you and your coworkers.

Start a free company trial today

More from MedWatch

Further reading

Related articles

Latest news

See all jobs