MedWatch

Orphazyme no longer expects EMA decision this year

Orphazyme will likely have to wait until sometime during the first quarter of 2022 to receive a decision from the European Medicines Agency on its key candidate arimoclomol as a treatment for Niemann-Pick disease type C, the company reports.

Photo: Orphazyme/PR

Biotech company Orphazyme, which is based in Copenhagen, Denmark, must arm itself with more patience.

On Tuesday, the company reported that it is now anticipating a final decision from the European Medicines Agency (EMA) on its leading candidate arimoclomol, meant to treat the metabolic disorder known as Niemann-Pick disease type C (NPC), in the first quarter of 2022.

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