European practitioners will gain new methods for treatment after the June meeting of the European Medicines Agency's (EMA) Committee for Medicinal Products for Human Use (CHMP) where the panel recommended several novel drug candidates and new indications for existing drugs.
Celgene's gene therapy Abecma (idecabtagene vicleucel) was for example nominated for conditional marketing authorization as a fourth-line therapy for bone marrow cancer. CHMP also had a positive view of Biomarin's Voxzogo (vosoritid) for the day-to-day treatment of children with achondroplasia. This drug might eventually challenge Transcon CNP, which is produced by Danish biotech firm Ascendis, if the latter reaches the market.
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