MedWatch

Sanofi gets first ever approval within Niemann-Pick as Japan green-lights drug

As the first country in the world, Japan has approved a treatment, Sanofi-developed Xenpozyme, for Niemann-Pick disease type A, also known as acid sphingomyelinase deficiency (ASMD).

Photo: Benoit Tessier/Reuters/Ritzau Scanpix

Sanofi is the first and only company in the world to receive an approval for a drug targeting the disease acid sphingomyelinase deficiency (ASMD), Sanofi reports in a press release.

This also makes Japan the first country in the world to approve a drug in this indication, as it was the Japanese health authority that granted Sanofi the approval for Xenpozyme (olipudase alfa) as a treatment for adults and children with non-central nervous system manifestations of ASMD.

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