Sanofi is the first and only company in the world to receive an approval for a drug targeting the disease acid sphingomyelinase deficiency (ASMD), Sanofi reports in a press release.
This also makes Japan the first country in the world to approve a drug in this indication, as it was the Japanese health authority that granted Sanofi the approval for Xenpozyme (olipudase alfa) as a treatment for adults and children with non-central nervous system manifestations of ASMD.
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