MedWatch

Biomarin's hemophilia drug meets all endpoints in phase III study

Biomarin has released results from a phase III trial of gene therapy valoctocogene roxaparvovec against severe hemophilia A.

On Sunday, Biotech company Biomarin publicized results from the largest study of a gene therapy hemophilia A treatment ever, at least according to the company itself.

A total of 134 patients have participated in the late-stage trial with the drug candidate valoctocogene roxaparvovec, which was rejected by the US Food and Drug Administration in August 2020 and is currently being evaluated by the European Medicines Agency (EMA).

Read the whole article

Get 14 days free access.

No credit card is needed, and you will not be automatically signed up for a paid subscription after the free trial.

  • Access all locked articles
  • Receive our daily newsletters
  • Access our app
An error has occured. Please try again later.

Get full access for you and your coworkers.

Start a free company trial today

More from MedWatch

Further reading

Related articles

Latest news

See all jobs