MedWatch

Orphazyme after FDA meeting: New phase II/III trial won't be necessary

No new phase II/III study is required pertaining to a potential US approval of the lead cnadidate arimoclomol, which is meant to treat Niemann-Pick disease type C, Chief Financial Officer at Orphazyme Anders Vadsholt tells MedWatch.

Photo: Orphazyme / PR

It appears that Orphazyme will steer clear of the worst case scenario on the path toward US approval with its lead candidate arimoclomol, a treatment for the neurodegenerative disease, Niemann-Pick disease type C (NPC).

Chief Financial Officer at Orphazyme Anders Vadsholt tells Medwatch that the US Food and Drug Administration (FDA) has returned to the company with no additional requirement for a new and costly phase II/III trial before the drug's resubmission. This comes after a June meeting between the FDA and the Copenhagen-based biotech company regarding the FDA's rejection of arimoclomol this summer.

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